CRISPR gene editing technology breakthrough may cure more diseases



Earlier, it has been proven that CRISPR gene editing technology can cure diseases that have left medical staff at a loss. However, in the past, this technology required direct genome editing tools into the affected cells, which limited the circumstances in which it could be used. But this problem has just got a breakthrough. According to NPR, researchers have published new research results, stating that they have successfully injected tools into the bloodstream of the body for gene editing, overcoming the limitations of the past, and turning many previously difficult diseases into It can be cured.

The target of this study is on patients suffering from a rare genetic disease “transthyretin amyloidosis.” Scientists inject genome editing tools into volunteers to attract and modify genes in the patient’s liver so that the organ will no longer release a harmful protein. Eventually, the indicators of the substance in the patient’s body plummet, saving them from this disease that can quickly destroy nerves and other tissues.

Although the results of this study were successful, because there were only six subjects, and the team still needs to verify the negative effects of this approach, this method has not been launched on the market immediately. If the final results indicate that this method will not have too many side effects, it will be applicable to chronic diseases that CRISPR cannot cope with, such as Alzheimer’s disease and heart disease.

On the other hand, some people have begun to worry that CRISPR will be abused by others, and there are a lot of moral problems such as “designing babies”. Although the genome editing tool is successfully imported into the body, there will be many uncertainties in its use, but as long as it is used properly, it can enable humans to avoid and prevent many previously insoluble diseases.

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